Columnist Helen Baldwin shares how her family joined the rare disease community after the diagnosis of her late son, Jeffrey, ...
Despite her initial reluctance to consult with a pain specialist, columnist Sherry Toh was pleased with the holistic help one ...
Spinraza treatment may help restore lipid balance to the cerebrospinal fluid (CSF) of children with SMA, according to a small ...
A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...
SMA newborn screening programs were available in 31 countries in 2023, covering about 7% of the world's newborns, per a study.