NHS England

Empowering healthcare professionals to support sickle cell carriers through informed conversations

NHS England » Empowering healthcare professionals to support sickle cell carriers through informed conversations ...
UrbanGeekz on MSN

How gene therapy could end sickle cell disease

For generations, Sickle Cell Disease has been a devastating illness affecting millions of people around the world, ...
Medical Xpress

Scientists identify potential new genetic target for sickle cell disease treatment

Scientists from Johns Hopkins Medicine and eight other institutions in the United States, Africa and Europe say they have identified a potential new gene target that could be edited to treat sickle ...

Fulcrum plummets 50% after scrapping lead sickle-cell drug on FDA concerns

June 2 (Reuters) - Shares of Fulcrum Therapeutics plunged 50% in premarket trading on Tuesday after the company said it would ...
Afro

Addressing sickle cell disease: The importance of genetic counseling

People are often encouraged to “know their status,” however this healthy habit can be applied to more than just safe-sex practices. Although they are not the only community who suffers with sickle ...

Fulcrum scraps sickle cell drug program after FDA raises cancer-risk concerns

June 1 (Reuters) - Fulcrum Therapeutics said on Monday it would stop developing its experimental sickle-cell disease drug after the U.S. Food and Drug Administration raised cancer-risk concerns, which ...

Stem cell transplantation found to be more cost-effective than gene therapy for sickle cell disease

Stem cell transplantation is the most cost-effective option for long-term care of sickle cell disease in adults when compared ...
Business Insider

Agios Submits sNDA to FDA for U.S. Accelerated Approval of Mitapivat in Sickle Cell Disease

Confirmatory trial designed to demonstrate clinical benefit of mitapivat on reducing transfusion burden in sickle cell disease CAMBRIDGE, Mass., May 12, 2026 (GLOBE NEWSWIRE) -- Agios Pharmaceuticals, ...