Analysis from continued follow-up of Phase 1/2 clinical trial data in Hunter syndrome (MPS II) reinforces potential for tividenofusp alfa ...
Functioning brain cells need a functioning system for picking up the trash and sorting the recycling. But when the cellular sanitation machines responsible for those tasks, called lysosomes, break ...
Ahmedabad: The city recently got the national biobank for lysosomal storage disorders at the FRIGE Institute of Human Genetics. Lysosomal storage disorders (LSDs) are a diverse group of over 70 rare, ...
Together with colleagues from Stanford University, USA, researchers at the Leibniz Institute on Aging (FLI) have, for the first time, created a comprehensive cell type-specific atlas of lysosomes in ...
Chiesi’s abstract presentations will focus on clinical insights and patient-reported outcomes in Fabry disease and ...
LONDON--(BUSINESS WIRE)--Technavio’s latest market research report on the global lysosomal storage diseases (LSDs) market provides an analysis of the most important trends expected to impact the ...
While the National Policy for Rare Diseases (NPRD 2021) has provided critical support, more than 100 children have now exhausted the Rs 50 lakh financial assistance limit.
JCR Pharmaceuticals Co., Ltd. (TSE 4552; "JCR"), a global specialty biopharmaceutical company dedicated to developing therapies for rare and genetic diseases, today announced the presentation of four ...
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