Sickle Cell Disease Competitive Landscape Report 2026: Comprehensive Analysis of Over 40 Companies and More Than 50 Drugs

Opportunities in the Sickle Cell Disease market include advancing gene-editing therapies like EDIT-301, expanding VOC-reducing treatments such as inclacumab, and exploring novel drug candidates like ...
STAT

Vertex’s CRISPR treatment for sickle cell disease hits unexpected roadblock

More than two years after its approval, only about 60 patients across the U.S., Middle East, and Europe have been treated with the gene-editing therapy. Specialists at four sickle centers told STAT ...
Monitor

New gene therapy offers hope to sickle cell patients

Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease ...
The American Journal of Managed Care

New Sickle Cell Therapies Highlight Equity Gaps and Treatment Progress

Recent therapies like hydroxyurea (Droxia, Bristol-Myers Squibb), the first FDA-approved drug for SCD in 1994, increase fetal hemoglobin (HbF), which, through unknown pathways, improves SCD symptoms ...
Hoodline

South Jersey Sickle Cell Sufferer Says One-Shot Gene Fix Erased His Pain

For most of his 20 years, a New Jersey man knew pain as a daily reality. Now, after a one-time CRISPR gene-editing treatment at Children's Hospital of Philadelphia, Austin Louis says he is finally ...
Medical Xpress

Gene therapy reduces stroke risk factors in sickle cell disease patients

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital. Many people with sickle ...
The Observer

Ugandan biotech unveils sickle cell cure millions can afford

At the weekend in Kampala, a piece of news landed that could reshape the future of one of the world’s most neglected diseases. The United States Patent and Trademark Office (USPTO) had accepted a ...
MM&M

Medicaid tries new approach with sickle cell: Companies get paid only if costly gene therapies work

Serenity Cole enjoyed Christmas last month relaxing with her family near her St. Louis home, making crafts and visiting friends. It was a contrast to how Cole, 18, spent part of the 2024 holiday ...
ABC7 San Francisco

FDA approves gene therapies for sickle cell disease, a 'functional cure' for many

The U.S. Food and Drug Administration (FDA) on Friday announced that it has approved Casgevy, the first CRISPR gene-editing therapy for sickle cell disease, paving the way for thousands of patients in ...
News Medical

Gene therapy shows promise for reducing stroke risk in patients with sickle cell disease

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital. Many people with sickle ...
KCUR 89.3 FM

Gene Therapy May Aid In Sickle Cell Disease Treatment

We've been hearing a lot of reporting recently about using the latest genetic technology to try and treat sickle cell disease. Scientists are also making progress using older DNA techniques to help ...